Browsing publications by Emma Heslop

Newcastle AuthorsTitleYearFull text
Emma Heslop
Professor Volker Straub
Professor Katherine Bushby
The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development2015
Emma Heslop
Professor Volker Straub
Dr Louise Johnston
Professor Katherine Bushby
The TREAT-NMD Advisory Committee for Therapeutics (TACT): An innovative de-risking model to foster orphan drug development2015
Rachel Thompson
Dr Louise Johnston
Dr Monica Ensini
Emma Heslop
Professor Katherine Bushby
et al.
RD-Connect: An Integrated Platform Connecting Databases, Registries, Biobanks and Clinical Bioinformatics for Rare Disease Research2014
Dr Pauline McCormack
Dr Simon Woods
Emma Heslop
Professor Volker Straub
Professor Katherine Bushby
et al.
Guidance in social and ethical issues related to clinical, diagnostic care and novel therapies for hereditary neuromuscular rare diseases: "translating" the translational2013
Emma Heslop
Dr Pauline McCormack
Professor Christoph Rehmann-Sutter
Dr Simon Woods
The risks of therapeutic misconception and individual patient (n = 1) “trials” in rare diseases such as Duchenne dystrophy2011
Professor Katherine Bushby
Emma Heslop
Dr Pauline McCormack
Dr Simon Woods
The development of antisense oligonucleotide therapies for Duchenne muscular dystrophy: Report on a TREAT-NMD workshop hosted by the European Medicines Agency (EMA), on September 25th 20092010
Emma Heslop
Dr Ali Aldibbiat
Dr Nicola Leech
Professor James Shaw
[abstract] Safety and efficacy of continuous subcutaneous insulin infusion therapy in relation to pre-intervention HbA1c2006