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Translating the Genomics Revolution: The Need for an International Gene Therapy Consortium for Monogenic Diseases

Lookup NU author(s): Professor Hanns Lochmuller

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Author(s): Tremblay JP, Xiao X, Aartsma-Rus A, Barbas C, Blaus HM, Bogdanove AJ, Boycott K, Brauns S, Breakefield XO, Bueren JA, Buschmann M, Byrne BJ, Calos M, Cathomen T, Chamberlain J, Chuah M, Cornetta K, Davies KE, Dickson JG, Duchateau P, Flotte TR, Gaudet D, Gersbach CA, Gilbert R, Glorioso J, Herzog RW, High KA, Huang WL, Huard J, Joung JK, Liu DP, Liu DX, Lochmuller H, Lustig L, Martens J, Massie B, Mavilio F, Mendell JR, Nathwani A, Ponder K, Porteus M, Puymirat J, Samulski J, Takeda S, Thrasher A, VandenDriessche T, Wei YQ, Wilson JM, Wilton SD, Wolfe JH, Gao GP

Publication type: Letter

Publication status: Published

Journal: Molecular Therapy

Year: 2013

Volume: 21

Issue: 2

Pages: 266-268

Print publication date: 01/02/2013

ISSN (print): 1525-0016

ISSN (electronic): 1525-0024

Publisher: NATURE PUBLISHING GROUP

URL: http://dx.doi.org/10.1038/mt.2013.4

DOI: 10.1038/mt.2013.4


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