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Browsing publications by Dr Ingrid Verhaart.

Newcastle AuthorsTitleYearFull text
Dr Ingrid Verhaart
Agata Robertson
Becca Leary
Dr Grace McMacken
Professor Hanns Lochmuller
et al.
A multi-source approach to determine SMA incidence and research ready population2017
Dr Ingrid Verhaart
Agata Robertson
Dr Ian Wilson
Professor Annemieke Aartsma-Rus
Dr Shona Cameron
et al.
Prevalence, incidence and carrier frequency of 5q-linked spinal muscular atrophy - A literature review2017
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
A 3-base pair deletion, c.9711_9713del, in DMD results in intellectual disability without muscular dystrophy2014
Dr Ingrid Verhaart
Low dystrophin levels in heart can delay heart failure in mdx mice2014
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
The dynamics of compound, transcript, and protein effects after treatment With 2OMePS antisense oligonucleotides in mdx mice2014
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
DMD transcript imbalance determines dystrophin levels2013
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
AON-Mediated Exon Skipping for Duchenne Muscular Dystrophy2012
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
Assessment of cardiac function in three mouse dystrophinopathies by magnetic resonance imaging2012
Dr Ingrid Verhaart
Circulating specific antibodies enhance systemic cross-priming by delivery of complexed antigen to dendritic cells in vivo 2012
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
Gene therapy for Duchenne muscular dystrophy2012
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
Prednisolone treatment does not interfere with 2'-O-methyl phosphorothioate antisense-mediated exon skipping in Duchenne muscular dystrophy2012
Dr Ingrid Verhaart
Professor Annemieke Aartsma-Rus
The effect of 6-thioguanine on alternative splicing and antisense-mediated exon skipping treatment for duchenne muscular dystrophy2012